TOGARAM1

TOG array regulator of axonemal 1

Ensembl:
ENSG00000198718
UniProt:
Q9Y4F4
OMIM:
617618
Synonyms:
CRESCERIN, CRESCERIN-1, FAM179B, KIAA0423

Cilia effects upon perturbation of TOGARAM1

Loss-of-function effect:
Shorter cilia

Phenotypes

Mouse phenotype:
abnormal craniofacial morphology, hemorrhage, abnormal limb bud morphology, pretal lethality prior to heart atrial septation, facial cleft, abnormal forebrain morphology, anophthalmia, preweaning lethality, complete penetrance
Mouse ciliopathy phenotype:
microphthalmia, polydactyly
Human ciliopathy phenotype:
Joubert syndrome 37; Joubert syndrome

Ciliopathy associations

  • Joubert Syndrome
  • Neural tube defects with ciliary dysfunction

Subcellular localization

basal body, cilia

Functional category

  • Ciliary assembly/disassembly
  • Actin & cytoskeleton regulation

Function

Mutated in JBTS37. TOGARAM1 localized along the ciliary axoneme in hTERT-RPE1 cells and was associated with longer cilia when knocked down. Binds directly to ARMC9, forming a protein module that localizes to microtubule-like structures at the centriole and proximal portion of the cilium. The interaction with ARMC9 mapped to the N-termi l protein of TOGARAM1 (32453716, 32747439).The length of cilia was normal in the FAP256-KO, reduced (by 16%) in CHE12-KO and increased (by 14%) in ARMC9-KO cells (PMID: 30217954).

Model organism evidence

C. elegans (3 references)

Defects in cilia structure and function result in a broad range of developmental and sensory disorders.

CHE-12 and DYF-11 are conserved ciliary proteins that function cell-autonomously and are continuously required for maintenance of cilium morphology and function.

PMIDs: 26378256, 18245347, 2428682